What are Small Molecule Correctors and Potentiators?
Small molecule correctors and potentiators are compounds designed to enhance the function of defective CFTR proteins. Correctors help in the proper folding and trafficking of the CFTR protein to the cell surface, while potentiators enhance the activity of the CFTR protein that is already at the cell surface. These molecules act as chemical catalysts to improve the efficiency and functionality of the CFTR protein.
